CEO and founder Rachel McMinn outlined the company’s progress toward a potential commercial launch for its lead gene therapy ...

Rett syndrome is a rare neurodevelopment disorder that leads to developmental regression, usually after a period of normal ...

Dosed multiple Rett syndrome patients in REVEAL pivotal trial of TSHA-102, with enrollment advancing across multiple sites; on track to complete ...

Q4 2025 Management View CEO Sean Nolan highlighted 2025 as "a year of significant execution" for Taysha, calling attention to "compelling REVEAL Phase I/II data across pediatric, adolescent and adult ...

Researchers have discovered a new way to increase a key brain protein damaged in Rett syndrome, a rare genetic disorder that affects thousands of children worldwide. Early studies in mice and ...

A team of researchers at Baylor College of Medicine and the Duncan Neurological Research Institute (Duncan NRI) at Texas Children's Hospital reports in Science Translational Medicine a potential new ...

The Food and Drug Administration on Friday approved the first treatment for Rett syndrome, a genetic disease mostly affecting girls that causes severe neurologic impairments, robbing them of the ...

ST. LOUIS, Mo. (Ivanhoe Newswire) – Imagine your toddler learning to walk and talk and then all of the sudden, your child stops and starts regressing inside of themselves. That’s what happens to ...

Paige Nues provides her closing thoughts regarding the treatment management of Rett syndrome. Paige Nues: We have never felt more optimistic than [at] any time in the Rett syndrome’s history in terms ...

SAN FRANCISCO--(BUSINESS WIRE)--Herophilus announced today that in vivo studies underway of its lead candidate HRP-12975 are funded in part by the Rett Syndrome Research Trust (RSRT). HRP-12975 is the ...

Rett syndrome is a neurodevelopmental disorder that primarily affects girls, most of whom have mutations in the transcription regulatory gene MECP2. However, mutations in MECP2 also have been ...